Drug discoveries & therapeutics · 2025 11 20
Elamipretide: The first cardiolipin-directed mitochondrial therapeutic for Barth syndrome approved under accelerated approval.
Letter
Open attributed record →Attributed PubMed bibliography
Elamipretide literature
14 selected PubMed bibliographic records connected to the reviewed Elamipretide identity. Identity matching connects these records; it does not summarize their findings or imply safety, effectiveness, or scientific agreement.
Bibliographic records
14 selected records.
Publication years
8 attributed years.
Attributed venues
13 distinct venues.
Publication chronology
Selected records
Molecular genetics and metabolism · 2025 08 11
Elamipretide in the Management of Barth Syndrome: Current Evidence and a Case Report.
Journal Article · Case Reports · Review
Open attributed record →European heart journal. Case reports · 2025 01 22
Expanded-access use of elamipretide in a newborn with Barth syndrome: a case report.
Case Reports · Journal Article
Open attributed record →Genetics in medicine open · 2024 06 22
Expanded-access use of elamipretide in a critically ill patient with Barth syndrome.
Journal Article
Open attributed record →Future cardiology · 2023 06 16
Temporal evolution of the heart failure phenotype in Barth syndrome and treatment with elamipretide.
Journal Article · Review · Research Support, Non-U.S. Gov't
Open attributed record →Orphanet journal of rare diseases · 2023 04 11
Identifying responders to elamipretide in Barth syndrome: Hierarchical clustering for time series data.
Randomized Controlled Trial · Journal Article · Research Support, Non-U.S. Gov't
Open attributed record →GeroScience · 2023 02 25
Intermittent treatment with elamipretide preserves exercise tolerance in aged female mice.
Journal Article · Research Support, N.I.H., Extramural · Research Support, Non-U.S. Gov't
Open attributed record →JIMD reports · 2022 09 21
Use of Elamipretide in patients assigned treatment in the compassionate use program: Case series in pediatric patients with rare orphan diseases.
Journal Article
Open attributed record →Heart failure reviews · 2022 01 17
Targeting mitochondrial dysfunction with elamipretide.
Journal Article · Review · Research Support, Non-U.S. Gov't
Open attributed record →Heart failure reviews · 2021 10 08
Elamipretide for Barth syndrome cardiomyopathy: gradual rebuilding of a failed power grid.
Journal Article · Review · Research Support, Non-U.S. Gov't
Open attributed record →Proceedings of the National Academy of Sciences of the United States of America · 2020 06 17
Mitochondrial protein interaction landscape of SS-31.
Journal Article · Research Support, N.I.H., Extramural · Research Support, Non-U.S. Gov't
Open attributed record →Journal of cachexia, sarcopenia and muscle · 2020 02 25
A randomized crossover trial of elamipretide in adults with primary mitochondrial myopathy.
Journal Article · Randomized Controlled Trial · Research Support, Non-U.S. Gov't
Open attributed record →Cardiovascular drugs and therapy · 2018 Aug
Abnormalities of Mitochondrial Dynamics in the Failing Heart: Normalization Following Long-Term Therapy with Elamipretide.
Journal Article
Open attributed record →Journal of the American Society of Nephrology : JASN · 2013 07 11
The mitochondrial-targeted compound SS-31 re-energizes ischemic mitochondria by interacting with cardiolipin.
Journal Article · Research Support, N.I.H., Extramural · Research Support, Non-U.S. Gov't
Open attributed record →